Definition of Zolgensma. Meaning of Zolgensma. Synonyms of Zolgensma

- Onasemnogene abeparvovec, sold under the brand name Zolgensma, is a gene therapy used to treat spinal muscular atrophy (SMA), a disease causing muscle...
- is diagnosed with spinal muscular atrophy and requires an injection of Zolgensma, which costs ₹17 crores. Saindhav goes back to the world of crime to extract...
- Strimvelis (2016), Kymriah (2017), Luxturna (2017), Onpattro (2018), Zolgensma (2019), Abecma (2021), Adstiladrin, Roctavian and Hemgenix (all 2022)...
- In 2019, AveXis's first gene therapy drug onasemnogene abeparvovec (Zolgensma) received regulatory approval in the United States and, with a list price...
- head of state to speed up the treatment of Brazilian twins with the drug Zolgensma, considered one of the most expensive and rare drugs in the world, which...
- Retrieved 1 June 2017. "Zolgensma 2 x 1013 vector genomes/mL solution for infusion". www.medicines.org.uk. Retrieved 8 August 2020. "Zolgensma- onasemnogene abeparvovec-xioi...
- in response to an FDA investigation about mani****ted data involving Zolgensma, Narasimhan defended the company's decision to delay informing the FDA...
- part of an attempt to gain the FDA's approval for its new gene therapy Zolgensma, writing that it was "unconscionable that a drug company would provide...
- part of an attempt to gain the FDA's approval for its new gene therapy Zolgensma, writing that it was "unconscionable that a drug company would provide...
- expensive drug, Zolgensma, costs over US$2.1 million per year of treatment, which are generally considered as unaffordable. Since Zolgensma is the only approved...