-
Ataluren, sold
under the
brand name Translarna, is a
medication for the
treatment of
Duchenne muscular dystrophy. It was
designed by PTC Therapeutics....
-
small molecule drugs such as
aminoglycosides and negamycin. An oxadiazole,
ataluren (previously PTC124),
facilitates the
selective read-through of aberrant...
-
currently available including gene
therapy (Elevidys), and
antisense drugs (
Ataluren,
Eteplirsen etc.).
Other medications used
include glucocorticoids (Deflazacort...
-
currently available including gene
therapy (Elevidys), and
antisense drugs (
Ataluren,
Eteplirsen etc.).
Other medications used
include glucocorticoids (Deflazacort...
- the FDA in 2015. As of 2015,
lumacaftor had no
medical use on its own.
Ataluren,
targeting premature stop
codons **** K, Taylor-Cousar JL (December 2015)...
-
approved drugs for
human illness therapy is scarce. Ribavirin, branaplam, and
ataluren are
currently available medications that
stabilize double-stranded RNA...
- to
dying muscle cells.
These patients do not
require antisense drugs (
Ataluren,
Eteplirsen etc.) as
certain percentage of
dystrophin is
already expressed...
- with PTC that
produced ataluren—Sweeney was the last
author on the
initial publication of
ataluren in
Nature in 2007.
Ataluren was
approved to
treat DMD...
- (deflazacort) from
Marathon Pharmaceuticals. PTC also owns Translarna, (
Ataluren)
marketed for
nonsense mutation Duchenne muscular dystrophy. Together,...
-
combinations M09AX01
Hyaluronic acid M09AX02 Chondrocytes,
autologous M09AX03
Ataluren M09AX04 Drisa****n M09AX05
Aceneuramic acid M09AX06
Eteplirsen M09AX07...
